Clinical improvement with JAK2 inhibition in Chuvash polycythemia

AW Zhou, EM Knoche, EK Engle… - … England Journal of …, 2016 - Mass Medical Soc
AW Zhou, EM Knoche, EK Engle, M Ban-Hoefen, C Kaiwar, ST Oh
New England Journal of Medicine, 2016Mass Medical Soc
Clinical Improvement with JAK2 Inhibition in Chuvash Polycythemia | NEJM Skip to main content
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Rare mutations in the VHL gene may lead to polycythemia in children. Ruxolitinib resulted in clinical improvement in three people with this disorder.
The New England Journal Of Medicine